AAV-Mediated Gene Therapy in the Guanylate Cyclase (RetGC1/RetGC2) Double Knockout Mouse Model of Leber Congenital Amaurosis-Reference-Cited by-同舟云学术

AAV-Mediated Gene Therapy in the Guanylate Cyclase (RetGC1/RetGC2) Double Knockout Mouse Model of Leber Congenital Amaurosis

Published:2013-02 Issue:2 Volume:24 Page:189-202
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Boye Sanford L.¹,Peshenko Igor V.²,Huang Wei Chieh³,Min Seok Hong¹,McDoom Issam¹,Kay Christine N.¹,Liu Xuan¹,Dyka Frank M.¹,Foster Thomas C.⁴,Umino Yumiko⁵,Karan Sukanya⁶,Jacobson Samuel G.³,Baehr Wolfgang⁶,Dizhoor Alexander²,Hauswirth William W.¹,Boye Shannon E.¹

Affiliation:

1. Department of Ophthalmology, College of Medicine, University of Florida, Gainesville, FL 32610.

2. Department of Basic Sciences and Pennsylvania College of Optometry, Salus University, Elkins Park, PA 19027.

3. Scheie Eye Institute, University of Pennsylvania, Philadelphia, PA 19104.

4. Department of Neuroscience, College of Medicine, University of Florida, Gainesville, FL 32610.

5. Department of Ophthalmology, College of Medicine, State University of New York (SUNY) Upstate Medical University, Syracuse, NY 13210.

6. Department of Ophthalmology, John A. Moran Eye Center, University of Utah Health Science Center, Salt Lake City, UT 84112.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2012.193

Reference82 articles.

1. HumanCRB1-Associated Retinal Degeneration: Comparison with therd8 Crb1-Mutant Mouse Model

2. Restoration of cone vision in a mouse model of achromatopsia

3. The human visual cortex responds to gene therapy–mediated recovery of retinal function

4. Fighting Blindness with Adeno-Associated Virus Serotype 8

5. The Function of Guanylate Cyclase 1 and Guanylate Cyclase 2 in Rod and Cone Photoreceptors

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