The human visual cortex responds to gene therapy–mediated recovery of retinal function-Reference-Cited by-同舟云学术

The human visual cortex responds to gene therapy–mediated recovery of retinal function

Published:2011-06-01 Issue:6 Volume:121 Page:2160-2168
ISSN:0021-9738
Container-title:Journal of Clinical Investigation
language:en
Short-container-title:J. Clin. Invest.

Author:

Ashtari Manzar,Cyckowski Laura L.,Monroe Justin F.,Marshall Kathleen A.,Chung Daniel C.,Auricchio Alberto,Simonelli Francesca,Leroy Bart P.,Maguire Albert M.,Shindler Kenneth S.,Bennett Jean

Publisher

American Society for Clinical Investigation

Subject

General Medicine

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1. Leber Congenital Amaurosis–A Model for Efficient Genetic Testing of Heterogeneous Disorders: LXIV Edward Jackson Memorial Lecture

2. Leber congenital amaurosis: Genes, proteins and disease mechanisms

3. Lighting a candle in the dark: advances in genetics and gene therapy of recessive retinal dystrophies

4. Mutations in RPE65 cause Leber's congenital amaurosis

5. Mutations in RPE65 cause autosomal recessive childhood–onset severe retinal dystrophy

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