Correction of Acidbeta-Galactosidase Deficiency in GM1Gangliosidosis Human Fibroblasts by Retrovirus VectorMediated Gene Transfer: Higher Efficiency of Release and Cross-Correction by the Murine Enzyme-Reference-Cited by-同舟云学术

Correction of Acidbeta-Galactosidase Deficiency in GM1Gangliosidosis Human Fibroblasts by Retrovirus VectorMediated Gene Transfer: Higher Efficiency of Release and Cross-Correction by the Murine Enzyme

Published:2000-03-20 Issue:5 Volume:11 Page:715-727
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Sena-Esteves Miguel,Camp Sara M.,Alroy Joseph,Breakefield Xandra O.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/10430340050015617

Reference61 articles.

1. Pathologic Findings in Fetal GM1 Gangliosidosis

2. Neonatal Intramuscular Injection with Recombinant Adeno-Associated Virus Results in Prolonged beta-Glucuronidase Expression in Situ and Correction of Liver Pathology in Mucopolysaccharidosis Type VII Mice

3. Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease

4. Molecular defect in combined beta-galactosidase and neuraminidase deficiency in man.

5. The Purification and Properties of β-Galactosidase from Bovine Testes

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