Neonatal Intramuscular Injection with Recombinant Adeno-Associated Virus Results in Prolonged beta-Glucuronidase Expression in Situ and Correction of Liver Pathology in Mucopolysaccharidosis Type VII Mice-Reference-Cited by-同舟云学术

Neonatal Intramuscular Injection with Recombinant Adeno-Associated Virus Results in Prolonged beta-Glucuronidase Expression in Situ and Correction of Liver Pathology in Mucopolysaccharidosis Type VII Mice

Published:1999-01 Issue:1 Volume:10 Page:85-94
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Daly Thomas M.,Okuyama Torayuki,Vogler Carole,Haskins Mark E.,Muzyczka Nicholas,Sands Mark S.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/10430349950019219

Reference37 articles.

1. Behavioral consequences of bone marrow transplantation in the treatment of murine mucopolysaccharidosis type VII.

2. Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency.

3. Increased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantation

4. Simultaneous Preparation and Quantitation of Proteoglycans by Precipitation with Alcian Blue

5. Complete sequence and organization of the murine .beta.-glucuronidase gene

Cited by 114 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Self-complementary AAV vector therapy for treating corneal cloudiness of mucopolysaccharidosis type VII (MPS VII);The Ocular Surface;2024-04

2. Recent Advances in In Vivo Somatic Cell Gene Modification in Newborn Pups;International Journal of Molecular Sciences;2023-10-18

3. Genome Integration of Adeno-associated Virus (AAV) Vectors into Infected Cells;Nihon Ika Daigaku Igakkai Zasshi;2023-08-31

4. Evaluating the state of the science for adeno-associated virus integration: An integrated perspective;Molecular Therapy;2022-08

5. Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence;Frontiers in Neurology;2022-01-05