Differences in the Human and Mouse Amino-Terminal Leader Peptides of Ornithine Transcarbamylase Affect Mitochondrial Import and Efficacy of Adenoviral Vectors-Reference-Cited by-同舟云学术

Differences in the Human and Mouse Amino-Terminal Leader Peptides of Ornithine Transcarbamylase Affect Mitochondrial Import and Efficacy of Adenoviral Vectors

Published:2001-06-10 Issue:9 Volume:12 Page:1035-1046
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Ye Xuehai¹,Zimmer Klaus-Peter²,Brown Rebecca³,Pabin Carol³,Batshaw Mark L.¹,Wilson James M.⁴,Robinson Michael B.³

Affiliation:

1. Children's National Medical Center and Department of Pediatrics, The George Washington University, Washington, D.C. 20010

2. Universitätskinderklinik, D-48149 Münster, Germany

3. Departments of Pediatrics and Pharmacology, University of Pennsylvania, Philadephia, PA 19104

4. Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/104303401750214267

Reference32 articles.

1. Treatment of Inborn Errors of Urea Synthesis

2. Risk of serious illness in heterozygotes for ornithine transcarbamylase deficency

3. Increase of ornithine transcarbamylase protein in sparse-fur mice with ortnithine transcarbamylase deficiency

4. The polypeptides of rat liver mitochondria: Identification of a 36,000 dalton polypeptide as the subunit of ornithine transcarbamylase

5. A new allele of the sparse fur gene in the mouse

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