Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome-Reference-Cited by-同舟云学术

Preclinical evaluation of a clinical candidate AAV8 vector for ornithine transcarbamylase (OTC) deficiency reveals functional enzyme from each persisting vector genome

Published:2012-02 Issue:2 Volume:105 Page:203-211
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Wang Lili,Morizono Hiroki,Lin Jianping,Bell Peter,Jones David,McMenamin Deirdre,Yu Hongwei,Batshaw Mark L.,Wilson James M.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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