Limited Transgene Immune Response and Long-Term Expression of Humanα-L-Iduronidase in Young Adult Mice with Mucopolysaccharidosis Type I by Liver-Directed Gene Therapy-Reference-Cited by-同舟云学术

Limited Transgene Immune Response and Long-Term Expression of Humanα-L-Iduronidase in Young Adult Mice with Mucopolysaccharidosis Type I by Liver-Directed Gene Therapy

Published:2006-11 Issue:11 Volume:17 Page:1112-1121
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Domenico C. Di¹²,Napoli D. Di³,Reyero E. Gonzalez Y³,Lombardo A.⁴,Naldini L.⁴,Natale P. Di¹

Affiliation:

1. Department of Biochemistry and Medical Biotechnologies, University of Naples Federico II, 80131 Naples, Italy.

2. CEINGE Advanced Biotechnologies, 80145 Naples, Italy.

3. Center for Animal Experimentation, Cardarelli Hospital Naples, 80128 Naples, Italy.

4. HSR-Telethon Institute for Gene Therapy, H. San Raffaele Scientific Institute, 20132 Milan, Italy.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2006.17.1112

Reference38 articles.

1. Simultaneous Preparation and Quantitation of Proteoglycans by Precipitation with Alcian Blue

2. Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease

3. Humoral immune response in mice against a circulating antigen induced by adenoviral transfer is strictly dependent on expression in antigen-presenting cells

4. Gene Therapy for a Mucopolysaccharidosis Type I Murine Model with Lentiviral-IDUA Vector

Cited by 35 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. MPSI Manifestations and Treatment Outcome: Skeletal Focus;International Journal of Molecular Sciences;2022-09-22

2. Promoter considerations in the design of lentiviral vectors for use in treating lysosomal storage diseases;Molecular Therapy - Methods & Clinical Development;2022-03

3. The systemic inflammatory landscape of COVID-19 in pregnancy: Extensive serum proteomic profiling of mother-infant dyads with in utero SARS-CoV-2;Cell Reports Medicine;2021-11

4. Effective Amelioration of Liver Fibrosis Through Lentiviral Vector Carrying Toxoplasma gondii gra15II in Murine Model;Frontiers in Immunology;2018-07-06

5. Liver-Directed Human Amniotic Epithelial Cell Transplantation Improves Systemic Disease Phenotype in Hurler Syndrome Mouse Model;Stem Cells Translational Medicine;2017-06-06