Gene Therapy for a Mucopolysaccharidosis Type I Murine Model with Lentiviral-IDUA Vector-Reference-Cited by-同舟云学术

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Gene Therapy for a Mucopolysaccharidosis Type I Murine Model with Lentiviral-IDUA Vector

Published:2005-01 Issue:1 Volume:16 Page:81-90
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Domenico Carmela Di¹,Villani Guglielmo R.D.¹,Napoli Daniele Di²,Reyero Enrico Gonzalez Y²,Lombardo Angelo³,Naldini Luigi³,Natale Paola Di¹

Affiliation:

1. Department of Biochemistry and Medical Biotechnologies, University of Naples Federico II, 80131 Naples, Italy.

2. Center for Animal Experimentation, Cardarelli Hospital, 80128 Naples, Italy.

3. HSR-Telethon Institute for Gene Therapy, H. San Raffaele Scientific Institute, 20132 Milan, Italy.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2005.16.81

Reference30 articles.

1. Simultaneous Preparation and Quantitation of Proteoglycans by Precipitation with Alcian Blue

2. Reversal of Pathology in the Entire Brain of Mucopolysaccharidosis Type VII Mice after Lentivirus-Mediated Gene Transfer

3. Functional correction of established central nervous system deficits in an animal model of lysosomal storage disease with feline immunodeficiency virus-based vectors

4. Dangerous liaisons: the role of “danger” signals in the immune response to gene therapy

5. Murine mucopolysaccharidosis type I: targeted disruption of the murine alpha-L-iduronidase gene

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