Comparison of Adeno-Associated Virus Pseudotype 1, 2, and 8 Vectors Administered by Intramuscular Injection in the Treatment of Murine Phenylketonuria-Reference-Cited by-同舟云学术

Comparison of Adeno-Associated Virus Pseudotype 1, 2, and 8 Vectors Administered by Intramuscular Injection in the Treatment of Murine Phenylketonuria

Published:2010-04 Issue:4 Volume:21 Page:463-477
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Rebuffat Alexandre¹,Harding Cary O.²,Ding Zhaobing¹³,Thöny Beat¹

Affiliation:

1. Division of Clinical Chemistry and Biochemistry, Department of Pediatrics, University of Zürich, CH-8032 Zürich, Switzerland.

2. Department of Molecular and Medical Genetics, Oregon Health and Science University, Portland, OR 97201, USA.

3. Present address: Institute of Bioengineering and Nanotechnology, The Nanos, 138669, Singapore.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2009.127

Reference78 articles.

1. Potential of AAV vectors in the treatment of metabolic disease

2. Timing is everything: Executive functions in children exposed to elevated levels of phenylalanine.

3. Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1

4. Bioluminescent virion shells: new tools for quantitation of AAV vector dynamics in cells and live animals

5. Intrahepatic Injection of Recombinant Adeno-Associated Virus Serotype 2 Overcomes Gender-Related Differences in Liver Transduction

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