Potential of AAV vectors in the treatment of metabolic disease
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.nature.com/articles/gt200864.pdf
Reference99 articles.
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2. Saudubray JM, Sedel F, Walter JH . Clinical approach to treatable inborn metabolic diseases: an introduction. J Inherit Metab Dis 2006; 29: 261274.
3. Boelens JJ . Trends in haematopoietic cell transplantation for inborn errors of metabolism. J Inherit Metab Dis 2006; 29: 413420.
4. Meyburg J, Hoffmann GF . Liver transplantation for inborn errors of metabolism. Transplantation 2005; 80: S135S137.
5. Fernandes J, Saudubray J-M, van den Berghe G (eds). Inborn Metabolic Diseases: Diagnosis and Treatment. 2nd edn. Springer-Verlag: Berlin, 1996.
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