Potential of AAV vectors in the treatment of metabolic disease

Author:

Alexander I E,Cunningham S C,Logan G J,Christodoulou J

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference99 articles.

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2. Saudubray JM, Sedel F, Walter JH . Clinical approach to treatable inborn metabolic diseases: an introduction. J Inherit Metab Dis 2006; 29: 261–274.

3. Boelens JJ . Trends in haematopoietic cell transplantation for inborn errors of metabolism. J Inherit Metab Dis 2006; 29: 413–420.

4. Meyburg J, Hoffmann GF . Liver transplantation for inborn errors of metabolism. Transplantation 2005; 80: S135–S137.

5. Fernandes J, Saudubray J-M, van den Berghe G (eds). Inborn Metabolic Diseases: Diagnosis and Treatment. 2nd edn. Springer-Verlag: Berlin, 1996.

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