Combined N-of-1 trials to investigate mexiletine in non-dystrophic myotonia using a Bayesian approach; study rationale and protocol-Reference-Cited by-同舟云学术

Combined N-of-1 trials to investigate mexiletine in non-dystrophic myotonia using a Bayesian approach; study rationale and protocol

Published:2015-03-25 Issue:1 Volume:15 Page:
ISSN:1471-2377
Container-title:BMC Neurology
language:en
Short-container-title:BMC Neurol

Author:

Stunnenberg Bas C,Woertman Willem,Raaphorst Joost,Statland Jeffrey M,Griggs Robert C,Timmermans Janneke,Saris Christiaan G,Schouwenberg Bas J,Groenewoud Hans M,Stegeman Dick F,van Engelen Baziel G M,Drost Gea,van der Wilt Gert Jan

Publisher

Springer Science and Business Media LLC

Subject

Neurology (clinical),General Medicine

Link

http://link.springer.com/article/10.1186/s12883-015-0294-4/fulltext.html

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4. Venance SL, Herr BE, Griggs RC. Challenges in the design and conduct of therapeutic trials in channel disorders. Neurotherapeutics. 2007;4(2):199–204.

5. Griggs RC, Batshaw M, Dunkle M, Gopal-Srivastava R, Kaye E, Krischer J, et al. Clinical research for rare disease: opportunities, challenges, and solutions. Mol Genet Metab. 2009;96(1):20–6.

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