Recent progress and considerations for AAV gene therapies targeting the central nervous system-Reference-Cited by-同舟云学术

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Recent progress and considerations for AAV gene therapies targeting the central nervous system

Published:2018-05-18 Issue:1 Volume:10 Page:
ISSN:1866-1947
Container-title:Journal of Neurodevelopmental Disorders
language:en
Short-container-title:J Neurodevelop Disord

Author:

Lykken Erik Allen,Shyng Charles,Edwards Reginald James,Rozenberg Alejandra,Gray Steven James

Funder

National Institute of Child Health and Human Development

Hannah's Hope Fund

University of Texas Southwestern Medical Center

Publisher

Springer Science and Business Media LLC

Subject

Cognitive Neuroscience,Clinical Neurology,Pathology and Forensic Medicine,Pediatrics, Perinatology, and Child Health

Link

http://link.springer.com/content/pdf/10.1186/s11689-018-9234-0.pdf

Reference120 articles.

1. Lentz TB, Gray SJ, Samulski RJ. Viral vectors for gene delivery to the central nervous system. Neurobiol Dis. 2012;48:179–88.

2. Kantor B, Bailey RM, Wimberly K, Kalburgi SN, Gray SJ. Methods for gene transfer to the central nervous system. Adv Genet. 2014;87:125–97.

3. Kantor B, McCown T, Leone P, Gray SJ. Clinical applications involving CNS gene transfer. Adv Genet. 2014;87:71–124.

4. Mastakov MY, Baer K, Symes CW, Leichtlein CB, Kotin RM, During MJ. Immunological aspects of recombinant adeno-associated virus delivery to the mammalian brain. J Virol. 2002;76:8446–54.

5. Rosenberg JB, Sondhi D, Rubin DG, Monette S, Chen A, Cram S, De BP, Kaminsky SM, Sevin C, Aubourg P, Crystal RG. Comparative efficacy and safety of multiple routes of direct CNS administration of adeno-associated virus gene transfer vector serotype rh.10 expressing the human arylsulfatase A cDNA to nonhuman primates. Hum Gene Ther Clin Dev. 2014;25:164–77.

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