Comparative Efficacy and Safety of Multiple Routes of Direct CNS Administration of Adeno-Associated Virus Gene Transfer Vector Serotype rh.10 Expressing the Human Arylsulfatase A cDNA to Nonhuman Primates-Reference-Cited by-同舟云学术

Comparative Efficacy and Safety of Multiple Routes of Direct CNS Administration of Adeno-Associated Virus Gene Transfer Vector Serotype rh.10 Expressing the Human Arylsulfatase A cDNA to Nonhuman Primates

Published:2014-09 Issue:3 Volume:25 Page:164-177
ISSN:2324-8637
Container-title:Human Gene Therapy Clinical Development
language:en
Short-container-title:Human Gene Therapy Clinical Development

Author:

Rosenberg Jonathan B.¹,Sondhi Dolan¹,Rubin David G.¹,Monette Sébastien²,Chen Alvin¹,Cram Sara¹,De Bishnu P.¹,Kaminsky Stephen M.¹,Sevin Caroline³⁴,Aubourg Patrick³⁴,Crystal Ronald G.¹

Affiliation:

1. Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065.

2. Tri-Institutional Laboratory of Comparative Pathology, Weill Cornell Medical College, Memorial Sloan-Kettering Cancer Center, and Rockefeller University, New York, NY 10065.

3. INSERM U986, University Paris-Descartes, 75005 Paris, France.

4. Neuropediatrics Unit, Bicêtre Hospital, Le Kremlin Bicêtre, 94275 Paris, France.

Publisher

Mary Ann Liebert Inc

Subject

Genetics(clinical)

Link

http://www.liebertpub.com/doi/pdf/10.1089/humc.2013.239

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