Author:
Yang Yang,Wang Lili,Bell Peter,McMenamin Deirdre,He Zhenning,White John,Yu Hongwei,Xu Chenyu,Morizono Hiroki,Musunuru Kiran,Batshaw Mark L,Wilson James M
Publisher
Springer Science and Business Media LLC
Subject
Biomedical Engineering,Molecular Medicine,Applied Microbiology and Biotechnology,Bioengineering,Biotechnology
Reference36 articles.
1. Cunningham, S.C., Dane, A.P., Spinoulas, A., Logan, G.J. & Alexander, I.E. Gene delivery to the juvenile mouse liver using AAV2/8 vectors. Mol. Ther. 16, 1081–1088 (2008).
2. Wang, L., Wang, H., Bell, P., McMenamin, D. & Wilson, J.M. Hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector. Hum. Gene Ther. 23, 533–539 (2012).
3. Batshaw, M.L., Tuchman, M., Summar, M., Seminara, J. & Members of the Urea Cycle Disorders Consortium. A longitudinal study of urea cycle disorders. Mol. Genet. Metab. 113, 127–130 (2014).
4. Lichter-Konecki, U., Caldovic, L., Morizono, H. & Simpson, K. Ornithine transcarbamylase deficiency (1993–2013). in GeneReviews (eds. Pagon, R.A. et al.)
http://www.ncbi.nlm.nih.gov/books/NBK154378/
(29 August 2013).
5. Ah Mew, N., Krivitzky, L., McCarter, R., Batshaw, M., Tuchman, M. & Urea Cycle Disorders Consortium of the Rare Diseases Clinical Research Network. Clinical outcomes of neonatal onset proximal versus distal urea cycle disorders do not differ. J. Pediatr. 162, 324–9.e1 (2013).
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