Construction and analysis of compact muscle-specific promoters for AAV vectors
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.nature.com/articles/gt2008104.pdf
Reference45 articles.
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2. Deconinck N, Ragot T, Marechal G, Perricaudet M, Gillis JM . Functional protection of dystrophic mouse (mdx) muscles after adenovirus-mediated transfer of a dystrophin minigene. Proc Natl Acad Sci USA 1996; 93: 3570–3574.
3. Chamberlain JS . Gene therapy of muscular dystrophy. Hum Mol Genet 2002; 11: 2355–2362.
4. Harper SQ, Hauser MA, DelloRusso C, Duan D, Crawford RW, Phelps SF et al. Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy. Nat Med 2002; 8: 253–261.
5. Sakamoto M, Yuasa K, Yoshimura M, Yokota T, Ikemoto T, Suzuki M et al. Micro-dystrophin cDNA ameliorates dystrophic phenotypes when introduced into mdx mice as a transgene. Biochem Biophys Res Commun 2002; 293: 1265–1272.
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