An engineered AAV targeting integrin alpha V beta 6 presents improved myotropism across species
Author:
Funder
Institut National de la Santé et de la Recherche Médicale
Publisher
Springer Science and Business Media LLC
Link
https://www.nature.com/articles/s41467-024-52002-4.pdf
Reference69 articles.
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2. Pupo, A. et al. AAV vectors: the rubik’s cube of human gene therapy. Mol. Ther. J. Am. Soc. Gene Ther. 30, 3515–3541 (2022).
3. Crudele, J. M. & Chamberlain, J. S. AAV-based gene therapies for the muscular dystrophies. Hum. Mol. Genet 28, R102–R107 (2019).
4. Duan, D. Systemic AAV micro-dystrophin gene therapy for duchenne muscular dystrophy. Mol. Ther. J. Am. Soc. Gene Ther. 26, 2337–2356 (2018).
5. Mack, D. L. et al. Systemic AAV8-mediated gene therapy drives whole-body correction of myotubular myopathy in dogs. Mol. Ther. J. Am. Soc. Gene Ther. 25, 839–854 (2017).
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