Merits of Combination Cortical, Subcortical, and Cerebellar Injections for the Treatment of Niemann-Pick Disease Type A-Reference-Cited by-同舟云学术

Merits of Combination Cortical, Subcortical, and Cerebellar Injections for the Treatment of Niemann-Pick Disease Type A

Published:2012-10 Issue:10 Volume:20 Page:1893-1901
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Bu Jie,Ashe Karen M,Bringas John,Marshall John,Dodge James C,Cabrera-Salazar Mario A,Forsayeth John,Schuchman Edward H,Bankiewicz Krystof S,Cheng Seng H,Shihabuddin Lamya S.,Passini Marco A

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Clinical protocol: gene therapy of Canavan disease: AAV-2 vector for neurosurgical delivery of aspartoacylase gene (ASPA) to the human brain;Janson;Hum Gene Ther,2002

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