Integration Frequency and Intermolecular Recombination of rAAV Vectors in Non-human Primate Skeletal Muscle and Liver-Reference-Cited by-同舟云学术

Integration Frequency and Intermolecular Recombination of rAAV Vectors in Non-human Primate Skeletal Muscle and Liver

Published:2012-06 Issue:6 Volume:20 Page:1177-1186
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Nowrouzi Ali,Penaud-Budloo Magalie,Kaeppel Christine,Appelt Uwe,Le Guiner Caroline,Moullier Philippe,Kalle Christof von,Snyder Richard O,Schmidt Manfred

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference39 articles.

1. LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1;Hacein-Bey-Abina;Science,2003

2. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1;Ott;Nat Med,2006

3. Gammaretrovirus-mediated correction of SCID-X1 is associated with skewed vector integration site distribution in vivo;Schwarzwaelder;J Clin Invest,2007

4. Genotoxicity of retroviral integration in hematopoietic cells;Nienhuis;Mol Ther,2006

5. AAV vector integration sites in mouse hepatocellular carcinoma;Donsante;Science,2007

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