Alpharetroviral Vector-mediated Gene Therapy for X-CGD: Functional Correction and Lack of Aberrant Splicing-Reference-Cited by-同舟云学术

Alpharetroviral Vector-mediated Gene Therapy for X-CGD: Functional Correction and Lack of Aberrant Splicing

Published:2013-03 Issue:3 Volume:21 Page:648-661
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Kaufmann Kerstin B.,Brendel Christian,Suerth Julia D.,Mueller-Kuller Uta,Chen-Wichmann Linping,Schwäble Joachim,Pahujani Shweta,Kunkel Hana,Schambach Axel,Baum Christopher,Grez Manuel

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference48 articles.

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5. Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease;Stein;Nat Med,2010

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