Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease-Reference-Cited by-同舟云学术

Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease

Published:2010-01-24 Issue:2 Volume:16 Page:198-204
ISSN:1078-8956
Container-title:Nature Medicine
language:en
Short-container-title:Nat Med

Author:

Stein Stefan,Ott Marion G,Schultze-Strasser Stephan,Jauch Anna,Burwinkel Barbara,Kinner Andrea,Schmidt Manfred,Krämer Alwin,Schwäble Joachim,Glimm Hanno,Koehl Ulrike,Preiss Carolin,Ball Claudia,Martin Hans,Göhring Gudrun,Schwarzwaelder Kerstin,Hofmann Wolf-Karsten,Karakaya Kadin,Tchatchou Sandrine,Yang Rongxi,Reinecke Petra,Kühlcke Klaus,Schlegelberger Brigitte,Thrasher Adrian J,Hoelzer Dieter,Seger Reinhard,von Kalle Christof,Grez Manuel

Publisher

Springer Science and Business Media LLC

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Link

http://www.nature.com/articles/nm.2088.pdf

Reference59 articles.

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2. Aiuti, A. et al. Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning. Science 296, 2410–2413 (2002).

3. Gaspar, H.B. et al. Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector. Lancet 364, 2181–2187 (2004).

4. Gaspar, H.B. et al. Successful reconstitution of immunity in ADA-SCID by stem cell gene therapy following cessation of PEG-ADA and use of mild preconditioning. Mol. Ther. 14, 505–513 (2006).

5. Aiuti, A. et al. Gene therapy for immunodeficiency due to adenosine deaminase deficiency. N. Engl. J. Med. 360, 447–458 (2009).

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