Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation-Reference-Cited by-同舟云学术

Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation

Published:2016 Issue: Volume:5 Page:e381
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Slijkerman Radulfus WN,Vaché Christel,Dona Margo,García-García Gema,Claustres Mireille,Hetterschijt Lisette,Peters Theo A,Hartel Bas P,Pennings Ronald JE,Millan José M,Aller Elena,Garanto Alejandro,Collin Rob WJ,Kremer Hannie,Roux Anne-Françoise,Van Wijk Erwin

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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