Morpholino Oligomer–Mediated Exon Skipping Averts the Onset of Dystrophic Pathology in the mdx Mouse

Author:

Fletcher Sue,Honeyman Kaite,Fall Abbie M,Harding Penny L,Johnsen Russell D,Steinhaus Joshua P,Moulton Hong M,Iversen Patrick L,Wilton Stephen D

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference48 articles.

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3. Gene therapy: the ‘pro-sense‘ approach to Duchenne muscular dystrophy;van Deutekom;Eur J Hum Genet,2005

4. Advances in Duchenne muscular dystrophy gene therapy;van Deutekom;Nat Rev Genet,2003

5. Clinical and molecular studies in Duchenne muscular dystrophy;Emery;Prog Clin Biol Res,1989

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