Antisense oligonucleotides in the treatment of Duchenne muscular dystrophy: Where are we now?
Author:
Publisher
Elsevier BV
Subject
Genetics (clinical),Neurology (clinical),Neurology,Pediatrics, Perinatology and Child Health
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3. Autoregulation of polypyrimidine tract binding protein by alternative splicing leading to nonsense-mediated decay;Wollerton;Mol Cell,2004
4. Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy;Aartsma-Rus;Neuromuscul Disord,2002
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