Phenotypic Correction of α-Sarcoglycan Deficiency by Intra-arterial Injection of a Muscle-specific Serotype 1 rAAV Vector-Reference-Cited by-同舟云学术

登录注册会员服务联系我们

Phenotypic Correction of α-Sarcoglycan Deficiency by Intra-arterial Injection of a Muscle-specific Serotype 1 rAAV Vector

Published:2007-01 Issue:1 Volume:15 Page:53-61
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Fougerousse Francoise,Bartoli Marc,Poupiot Jérôme,Arandel Ludovic,Durand Muriel,Guerchet Nicolas,Gicquel Evelyne,Danos Olivier,Richard Isabelle

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference38 articles.

1. Disorders of Voluntary Muscle;Karpati,2001

2. Primary adhalinopathy (α-sarcoglycanopathy): clinical, pathological and genetic correlation in twenty patients with autosomal recessive muscular dystrophy;Eymard;Neurology,1997

3. Therapy insight: cardiovascular complications associated with muscular dystrophies;McNally;Nat Clin Pract Cardiovasc Med,2005

4. Primary structure and muscle-specific expression of the 50-kDa dystrophin-associated glycoprotein (adhalin);Roberds;J Biol Chem,1993

5. Missense mutations in the adhalin gene linked to autosomal recessive muscular dystrophy;Roberds;Cell,1994

Cited by 59 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Various AAV Serotypes and Their Applications in Gene Therapy: An Overview;Cells;2023-03-01

2. Les sarcoglycanopathies;médecine/sciences;2020-12

3. Of rAAV and Men: From Genetic Neuromuscular Disorder Efficacy and Toxicity Preclinical Studies to Clinical Trials and Back;Journal of Personalized Medicine;2020-11-28

4. New Therapeutics Options for Pediatric Neuromuscular Disorders;Frontiers in Pediatrics;2020-11-23

5. Mesenchymal Stem Cells: A New Generation of Therapeutic Agents as Vehicles in Gene Therapy;Current Gene Therapy;2020-11-13

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号京ICP备18003416号-3