Design of Tissue-specific Regulatory Cassettes for High-level rAAV-mediated Expression in Skeletal and Cardiac Muscle-Reference-Cited by-同舟云学术

Design of Tissue-specific Regulatory Cassettes for High-level rAAV-mediated Expression in Skeletal and Cardiac Muscle

Published:2007-02 Issue:2 Volume:15 Page:320-329
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Salva Maja Z,Himeda Charis L,Tai Phillip WL,Nishiuchi Eiko,Gregorevic Paul,Allen James M,Finn Eric E,Nguyen Quynh G,Blankinship Michael J,Meuse Leonard,Chamberlain Jeffrey S,Hauschka Stephen D

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference46 articles.

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3. Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart;Wang;Nat Biotech,2005

4. Sustained whole-body functional rescue in congestive heart failure and muscular dystrophy hamsters by systemic gene transfer;Zhu;Circulation,2005

5. Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein;Kessler;Proc Natl Acad Sci USA,1996

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