Complete Correction of Enzymatic Deficiency and Neurochemistry in the GM1-gangliosidosis Mouse Brain by Neonatal Adeno-associated Virus–mediated Gene Delivery-Reference-Cited by-同舟云学术

Complete Correction of Enzymatic Deficiency and Neurochemistry in the GM1-gangliosidosis Mouse Brain by Neonatal Adeno-associated Virus–mediated Gene Delivery

Published:2007-01 Issue:1 Volume:15 Page:30-37
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Broekman M L D,Baek R C,Comer L A,Fernandez J L,Seyfried T N,Sena-Esteves M

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference43 articles.

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3. Cerebral GM1-gangliosidosis: chemical pathology of visceral organs;Suzuki;Science,1968

4. Prenatal diagnosis of GM1-gangliosidosis: biochemical manifestations in fetal tissues;Kudoh;Hum Genet,1978

5. Pathologic findings in fetal GM1 gangliosidosis;Bieber;Arch Neurol,1986

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