Liver Production of Sulfamidase Reverses Peripheral and Ameliorates CNS Pathology in Mucopolysaccharidosis IIIA Mice-Reference-Cited by-同舟云学术

Liver Production of Sulfamidase Reverses Peripheral and Ameliorates CNS Pathology in Mucopolysaccharidosis IIIA Mice

Published:2012-02 Issue:2 Volume:20 Page:254-266
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Ruzo Albert,Garcia Miquel,Ribera Albert,Villacampa Pilar,Haurigot Virginia,Marcó Sara,Ayuso Eduard,Anguela Xavier M,Roca Carles,Agudo Judith,Ramos David,Ruberte Jesús,Bosch Fatima

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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4. Characterization of a C57BL/6 congenic mouse strain of mucopolysaccharidosis type IIIA;Crawley;Brain Res,2006

5. A mouse model for mucopolysaccharidosis type III A (Sanfilippo syndrome);Bhaumik;Glycobiology,1999

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