Ex Vivo and In Vivo Gene Therapy for Mucopolysaccharidoses: State of the Art
Author:
Funder
Fondazione Telethon
Publisher
Elsevier BV
Subject
Oncology,Hematology
Reference61 articles.
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3. Enzyme replacement combinational therapy: effective treatments for mucopolysaccharidoses;Safary;Expert Opin Biol Ther,2021
4. Therapy for the mucopolysaccharidoses;Valayannopoulos;Rheumatology (Oxford),2011
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