Potent and Selective Antisense Oligonucleotides Targeting Single-Nucleotide Polymorphisms in the Huntington Disease Gene / Allele-Specific Silencing of Mutant Huntingtin-Reference-Cited by-同舟云学术

Potent and Selective Antisense Oligonucleotides Targeting Single-Nucleotide Polymorphisms in the Huntington Disease Gene / Allele-Specific Silencing of Mutant Huntingtin

Published:2011-12 Issue:12 Volume:19 Page:2178-2185
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Carroll Jeffrey B,Warby Simon C,Southwell Amber L,Doty Crystal N,Greenlee Sarah,Skotte Niels,Hung Gene,Bennett C Frank,Freier Susan M,Hayden Michael R

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference48 articles.

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5. Levels of mutant huntingtin influence the phenotypic severity of Huntington disease in YAC128 mouse models;Graham;Neurobiol Dis,2006

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