Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT
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Published:2024-09
Issue:3
Volume:35
Page:102246
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ISSN:2162-2531
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Container-title:Molecular Therapy - Nucleic Acids
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language:en
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Short-container-title:Molecular Therapy - Nucleic Acids
Author:
Iwamoto Naoki, Liu Yuanjing, Frank-Kamenetsky Maria, Maguire Abbie, Tseng Wei Chou, Taborn Kristin, Kothari Nayantara, Akhtar Ali, Bowman Keith, Shelke Juili Dilip, Lamattina Anthony, Hu Xiao Shelley, Jang Hyun Gyung, Kandasamy Pachamuthu, Liu Fangjun, Longo Ken, Looby Richard, Meena , Metterville Jake, Pan Qianli, Purcell-Estabrook Erin, Shimizu Mamoru, Prakasha Priyanka Shiva, Standley Stephany, Upadhyay Hansini, Yang Hailin, Yin Yuan, Zhao Anderson, Francis Christopher, Byrne Mike, Dale Elena, Verdine Gregory L., Vargeese ChandraORCID
Cited by
1 articles.
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