Publisher
Springer Science and Business Media LLC
Reference12 articles.
1. Finkel, R.S. et al. Lancet 388, 3017–3026 (2016).
2. US Food & Drug Administration. Spinraza (nusinersen) injection.
http://www.accessdata.fda.gov/drugsatfda_docs/nda/2016/209531Orig1s000TOC.cfm
(2016).
3. Faravelli, I., Nizzardo, M., Comi, G.P. & Corti, S. Nat. Rev. Neurol. 11, 351–359 (2015).
4. Cartegni, L. & Krainer, A.R. Nat. Genet. 30, 377–384 (2002).
5. Havens, M.A. & Hastings, M.L. Nucleic Acids Res. 44, 6549–6563 (2016).
Cited by
191 articles.
订阅此论文施引文献
订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献