Gene Insertion Into Genomic Safe Harbors for Human Gene Therapy
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine
Reference71 articles.
1. Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy;Cartier;Science,2009
2. Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction;Gaspar;Sci Transl Med,2011
3. A modified γ-retrovirus vector for X-linked severe combined immunodeficiency;Hacein-Bey-Abina;N Engl J Med,2014
4. Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy;Biffi;Science,2013
5. Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome;Aiuti;Science,2013
Cited by 184 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Saponin and fluorine-functionalized polyethyleneimine/covered metal organic framework: A novel gene delivery system for targeted delivery of green fluorescent protein plasmid;Journal of Drug Delivery Science and Technology;2024-10
2. Adeno-Associated Virus Vectors—a Target of Cellular and Humoral Immunity—are Expanding Their Reach Toward Hematopoietic Stem Cell Modification and Immunotherapies;Human Gene Therapy;2024-08-28
3. STRAIGHT-IN: a platform for rapidly generating panels of genetically modified human pluripotent stem cell lines;Nature Protocols;2024-08-23
4. Regulatory Considerations for Genome-Edited T-cell Therapies;Cancer Immunology Research;2024-07-16
5. A review of advances in integrating gene regulatory networks and metabolic networks for designing strain optimization;Journal of King Saud University - Computer and Information Sciences;2024-07
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3