Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapy-Reference-Cited by-同舟云学术

Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapy

Published:2019-05-31 Issue:12 Volume:54 Page:1995-2003
ISSN:0268-3369
Container-title:Bone Marrow Transplantation
language:en
Short-container-title:Bone Marrow Transplant

Author:

Tucci Francesca^ORCID,Frittoli Marta,Barzaghi Federica,Calbi Valeria,Migliavacca Maddalena,Ferrua Francesca,Fumagalli Francesca,Lorioli Laura,Castagnaro Laura,Facchini Marcella,Fossati Claudia,Zancan Stefano,Massariello Paola,Manfredini Michele,Consiglieri Giulia,Canarutto Daniele,Recupero Salvatore,Calzatini Francesco,Casiraghi Miriam,Darin Silvia,Antonioli Gigliola,Miniero Roberto^ORCID,Fiori Rossana,Silvani Paolo,Zambelli Matilde,Marktel Sarah,Gattillo Salvatore,Milani Raffaella,Santoleri Luca,Ciceri Fabio,Biffi Alessandra,Cicalese Maria Pia,Bernardo Maria Ester,Aiuti Alessandro

Publisher

Springer Science and Business Media LLC

Subject

Transplantation,Hematology

Link

http://www.nature.com/articles/s41409-019-0573-6.pdf

Reference26 articles.

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2. Gaspar HB, Cooray S, Gilmour KC, Parsley KL, Zhang F, Adams S, et al. Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction. Sci Transl Med. 2011;3:97ra80.

3. Candotti F, Shaw KL, Muul L, Carbonaro D, Sokolic R, Choi C, et al. Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans. Blood. 2012;120:3635–46.

4. Cicalese MP, Ferrua F, Castagnaro L, Pajno R, Barzaghi F, Giannelli S, et al. Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency. Blood. 2016;128:45–54.

5. Aiuti A, Biasco L, Scaramuzza S, Ferrua F, Cicalese MP, Baricordi C, et al. Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome. Science. 2013;23:341. (6148):1233151

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