Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapy-Reference-Cited by-同舟云学术

Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapy

Published:2019-05-31 Issue:12 Volume:54 Page:1995-2003
ISSN:0268-3369
Container-title:Bone Marrow Transplantation
language:en
Short-container-title:Bone Marrow Transplant

Author:

Tucci Francesca^ORCID,Frittoli Marta,Barzaghi Federica,Calbi Valeria,Migliavacca Maddalena,Ferrua Francesca,Fumagalli Francesca,Lorioli Laura,Castagnaro Laura,Facchini Marcella,Fossati Claudia,Zancan Stefano,Massariello Paola,Manfredini Michele,Consiglieri Giulia,Canarutto Daniele,Recupero Salvatore,Calzatini Francesco,Casiraghi Miriam,Darin Silvia,Antonioli Gigliola,Miniero Roberto^ORCID,Fiori Rossana,Silvani Paolo,Zambelli Matilde,Marktel Sarah,Gattillo Salvatore,Milani Raffaella,Santoleri Luca,Ciceri Fabio,Biffi Alessandra,Cicalese Maria Pia,Bernardo Maria Ester,Aiuti Alessandro

Publisher

Springer Science and Business Media LLC

Subject

Transplantation,Hematology

Link

http://www.nature.com/articles/s41409-019-0573-6.pdf

Reference26 articles.

1. Aiuti A, Cattaneo F, Galimberti S, Benninghoff U, Cassani B, Callegaro L, et al. Gene therapy for immunodeficiency due to adenosine deaminase deficiency. N Engl J Med. 2009;360:447–58.

2. Gaspar HB, Cooray S, Gilmour KC, Parsley KL, Zhang F, Adams S, et al. Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction. Sci Transl Med. 2011;3:97ra80.

3. Candotti F, Shaw KL, Muul L, Carbonaro D, Sokolic R, Choi C, et al. Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans. Blood. 2012;120:3635–46.

4. Cicalese MP, Ferrua F, Castagnaro L, Pajno R, Barzaghi F, Giannelli S, et al. Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency. Blood. 2016;128:45–54.

5. Aiuti A, Biasco L, Scaramuzza S, Ferrua F, Cicalese MP, Baricordi C, et al. Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome. Science. 2013;23:341. (6148):1233151

Cited by 9 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency;Nature Medicine;2024-02

2. Gene therapy for adenosine deaminase severe combined immune deficiency—An unexpected journey of four decades;Immunological Reviews;2023-11-30

3. Updates on Severe Combined Immunodeficiency;Common Pediatric Diseases: an Updated Review;2022-04-13

4. Peripheral blood stem and progenitor cell collection in pediatric candidates for ex vivo gene therapy: a 10-year series;Molecular Therapy - Methods & Clinical Development;2021-09

5. Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposes;Molecular Therapy - Methods & Clinical Development;2021-09