1. San Raffaele Telethon Institute for Gene Therapy, San Raffaele Scientific Institute, Milan, Italy;
2. Pediatric Immunohematology and Bone Marrow Transplantation Unit, San Raffaele Scientific Institute, Milan, Italy;
3. Vita-Salute San Raffaele University, Milan, Italy;
4. Department of Medical Biotechnology, University of Siena, Siena, Italy;
5. Division of Immunology and Allergy, The Hospital for Sick Children, Toronto, Canada;
6. Division of Immunology and Allergy, Hamad Medical Corporation, Doha, Qatar;
7. Department of Pediatrics, Leiden University Medical Center, Leiden, The Netherlands;
8. Department of Pediatrics, University of California–San Francisco, San Francisco, CA;
9. Pediatric Hematology-Oncology and Bone Marrow Transplantation, Hadassah Hebrew University Hospital, Jerusalem, Israel;
10. Department of Pediatrics, Section of Pediatric Immunology, Hacettepe University Faculty of Medicine, Ankara, Turkey;
11. GSK Research and Development, GlaxoSmithKline, Stevenage, United Kingdom, and Upper Merion, PA;
12. Hematology and Bone Marrow Transplant Unit, San Raffaele Scientific Institute, Milan, Italy; and
13. Department of Pediatrics Division of Stem Cell Transplantation and Regenerative Medicine, and
14. Institute for Stem Cell Biology and Regenerative Medicine, Stanford University, Stanford, CA