Author:
Messina C,Rampazzo A,Cesaro S,Monciotti C,Gasparotto N,Tomanin R,Scarpa M
Publisher
Springer Science and Business Media LLC
Subject
Transplantation,Hematology
Reference4 articles.
1. Neufeld EF, Muenzer J . The Mucopolysaccharidoses. In: Scriver CR, Beaudet AL, Sly WS, Valle D (eds). The Metabolic and Molecular Bases of Inherited Disease, 8th edn, vol. III. McGraw-Hill: New York, 2001, pp 3421–3452.
2. Hobbs JR, Hugh-Jones K, Barrett AJ, Byrom N, Chambers D, Henry K et al. Reversal of clinical features of Hurler's disease and biochemical improvement after treatment by bone-marrow transplantation. Lancet 1981; 2: 709–712.
3. Peters C, Steward CG . Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines. Bone Marrow Transplant 2003; 31: 229–239.
4. Wraith JE . The first 5 years of clinical experience with laronidase enzyme replacement therapy for mucopolysaccharidosis I. Expert Opin Pharmacother 2005; 6: 489–506.
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