Potential lifetime quality of life benefits of choroideremia gene therapy: projections from a clinically informed decision model-Reference-Cited by-同舟云学术

Potential lifetime quality of life benefits of choroideremia gene therapy: projections from a clinically informed decision model

Published:2019-07-17 Issue:8 Volume:33 Page:1215-1223
ISSN:0950-222X
Container-title:Eye
language:en
Short-container-title:Eye

Author:

Halioua-Haubold Celine-Lea,Jolly Jasleen K.^ORCID,Smith James A.^ORCID,Pinedo-Villanueva Rafael^ORCID,Brindley David A.,MacLaren Robert E.

Publisher

Springer Science and Business Media LLC

Subject

Ophthalmology

Link

http://www.nature.com/articles/s41433-019-0492-1.pdf

Reference22 articles.

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2. Sangonowsky E Spark sets off gene therapy debate with $850K sticker on Luxturna | FiercePharma. FiercePharma. /pharma/spark-prices-gene-therapy-luxturna-at-850k-grabbing-top-spot-pharma-s-costliest-drugs. Published 3 January 3, 2018. Accessed 25 January2018.

3. NICE. Evaluation Consultation Document: Strimvelis for Treating Adenosine Deaminase Deficiency–Severe Combined Immunodeficiency.; 2017. https://www.nice.org.uk/guidance/GID-HST10005/documents/evaluation-consultation-document . Accessed October 25, 2017.

4. Touchot N, Flume M. Early Insights from Commercialization of Gene Therapies in Europe. Genes. 2017;8:78.

5. SEC Filings | Investors & Media | Spark Therapeutics. http://ir.sparktx.com/phoenix.zhtml?c=253900&p=irol-SECText&TEXT=aHR0cDovL2FwaS50ZW5rd2l6YXJkLmNvbS9maWxpbmcueG1sP2lwYWdlPTEwMTcwNDk3JkRTRVE9MSZTRVE9MTQmU1FERVNDPVNFQ1RJT05fUEFHRSZleHA9JnN1YnNpZD01Nw%3D%3D . Accessed 25 October 2017.

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