Review of gene therapies for age-related macular degeneration
Author:
Publisher
Springer Science and Business Media LLC
Subject
Ophthalmology
Link
https://www.nature.com/articles/s41433-021-01842-1.pdf
Reference77 articles.
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4. Hacein-Bey-Abina S, von Kalle C, Schmidt M, Le Deist F, Wulffraat N, McIntyre E, et al. A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency. N. Engl J Med. 2003;348:255–6.
5. Dunbar CE, High KA, Joung JK, Kohn DB, Ozawa K, Sadelain, M. Gene therapy comes of age. Science. 2018;359.
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