Bioengineered coagulation factor VIII enables long-term correction of murine hemophilia A following liver-directed adeno-associated viral vector delivery-Reference-Cited by-同舟云学术

Bioengineered coagulation factor VIII enables long-term correction of murine hemophilia A following liver-directed adeno-associated viral vector delivery

Published:2014 Issue: Volume:1 Page:14036
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Brown Harrison C,Wright J Fraser,Zhou Shangzhen,Lytle Allison M,Shields Jordan E,Spencer H Trent,Doering Christopher B

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference44 articles.

1. rAAV human trial experience;High;Methods Mol Biol,2011

2. Biosynthesis, assembly and secretion of coagulation factor VIII;Kaufman;Blood Coagul Fibrinolysis,1997

3. Quantitative analysis of the packaging capacity of recombinant adeno-associated virus;Dong;Hum Gene Ther,1996

4. Packaging capacity of adeno-associated virus serotypes: impact of larger genomes on infectivity and postentry steps;Grieger;J Virol,2005

5. Incidence of development of factor VIII and factor IX inhibitors in haemophiliacs;Ehrenforth;Lancet,1992

Cited by 36 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Deciphering conundrums of adeno-associated virus liver-directed gene therapy: focus on hemophilia;Journal of Thrombosis and Haemostasis;2023-12

2. Looking to the future of gene therapy for hemophilia A and B;Expert Review of Hematology;2023-10-11

3. Comparison of different gene addition strategies to modify placental derived-mesenchymal stromal cells to produce FVIII;Frontiers in Immunology;2022-12-15

4. Molecular therapeutics of hemophilia A and B;Expert Review of Hematology;2022-05-04

5. Pharmacokinetic analysis identifies a factor VIII immunogenicity threshold after AAV gene therapy in hemophilia A mice;Blood Advances;2022-04-22