Cell therapy for diverse central nervous system disorders: inherited metabolic diseases and autism
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pediatrics, Perinatology and Child Health
Link
http://www.nature.com/articles/pr2017254.pdf
Reference72 articles.
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3. Dickson PI, Kaitila I, Harmatz P et al. Safety of laronidase delivered into the spinal canal for treatment of cervical stenosis in mucopolysaccharidosis I. Mol Genet Metab 2015;116:69–74.
4. Valenzano KJ, Khanna R, Powe AC et al. Identification and characterization of pharmacological chaperones to correct enzyme deficiencies in lysosomal storage disorders. Assay Drug Dev Technol 2011;9:213–235.
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