Identification and Characterization of Pharmacological Chaperones to Correct Enzyme Deficiencies in Lysosomal Storage Disorders
Author:
Affiliation:
1. Amicus Therapeutics, Cranbury, New Jersey.
2. ArunA Biomedical, Inc., Athens, Georgia.
Publisher
Mary Ann Liebert Inc
Subject
Drug Discovery,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/adt.2011.0370
Reference197 articles.
1. Lysosomale Speichererkrankungen - Update und neue therapeutische Optionen
2. Lysosomal Storage Disease: Revealing Lysosomal Function and Physiology
3. A counterintuitive approach to treat enzyme deficiencies: use of enzyme inhibitors for restoring mutant enzyme activity
4. Lysosomal Storage Disorders in the Newborn
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