CRISPR–Cas9-mediated gene editing of the BCL11A enhancer for pediatric β0/β0 transfusion-dependent β-thalassemia-Reference-Cited by-同舟云学术

CRISPR–Cas9-mediated gene editing of the BCL11A enhancer for pediatric β0/β0 transfusion-dependent β-thalassemia

Published:2022-08 Issue:8 Volume:28 Page:1573-1580
ISSN:1078-8956
Container-title:Nature Medicine
language:en
Short-container-title:Nat Med

Author:

Fu Bin^ORCID,Liao Jiaoyang^ORCID,Chen Shuanghong,Li Wei^ORCID,Wang Qiudao,Hu Jian,Yang Fei,Hsiao Shenlin,Jiang Yanhong,Wang Liren,Chen Fangping,Zhang Yuanjin,Wang Xin^ORCID,Li Dali^ORCID,Liu Mingyao^ORCID,Wu Yuxuan^ORCID

Publisher

Springer Science and Business Media LLC

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Link

https://www.nature.com/articles/s41591-022-01906-z.pdf

Reference30 articles.

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2. Cao, A. & Galanello, R. Beta-thalassemia. Genet. Med. 12, 61–76 (2010).

3. Taher, A. T., Weatherall, D. J. & Cappellini, M. D. Thalassaemia. Lancet 391, 155–167 (2018).

4. Thein, S. L. The molecular basis of β-thalassemia. Cold Spring Harb. Perspect. Med. 3, a011700 (2013).

5. Yin, X. L. et al. Treatment and complications of thalassemia major in Guangxi, Southern China. Pediatr. Blood Cancer 57, 1174–1178 (2011).

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