Gene Therapy Using a Liver-targeted AAV Vector Restores Nucleoside and Nucleotide Homeostasis in a Murine Model of MNGIE-Reference-Cited by-同舟云学术

Gene Therapy Using a Liver-targeted AAV Vector Restores Nucleoside and Nucleotide Homeostasis in a Murine Model of MNGIE

Published:2014-05 Issue:5 Volume:22 Page:901-907
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Torres-Torronteras Javier,Viscomi Carlo,Cabrera-Pérez Raquel,Cámara Yolanda,Di Meo Ivano,Barquinero Jordi,Auricchio Alberto,Pizzorno Giuseppe,Hirano Michio,Zeviani Massimo,Martí Ramon

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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4. Mitochondrial DNA depletion and thymidine phosphate pool dynamics in a cellular model of mitochondrial neurogastrointestinal encephalomyopathy;Pontarin;J Biol Chem,2006

5. Unbalanced deoxynucleotide pools cause mitochondrial DNA instability in thymidine phosphorylase-deficient mice;López;Hum Mol Genet,2009

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