An AAVS1-Targeted Minigene Platform for Correction of iPSCs From All Five Types of Chronic Granulomatous Disease-Reference-Cited by-同舟云学术

An AAVS1-Targeted Minigene Platform for Correction of iPSCs From All Five Types of Chronic Granulomatous Disease

Published:2015-01 Issue:1 Volume:23 Page:147-157
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Merling Randall K,Sweeney Colin L,Chu Jessica,Bodansky Aaron,Choi Uimook,Priel Debra Long,Kuhns Douglas B,Wang Hongmei,Vasilevsky Sam,De Ravin Suk See,Winkler Thomas,Dunbar Cynthia E,Zou Jizhong,Zarember Kol A,Gallin John I,Holland Steven M,Malech Harry L

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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