Myeloid/Microglial Driven Autologous Hematopoietic Stem Cell Gene Therapy Corrects a Neuronopathic Lysosomal Disease-Reference-Cited by-同舟云学术

Myeloid/Microglial Driven Autologous Hematopoietic Stem Cell Gene Therapy Corrects a Neuronopathic Lysosomal Disease

Published:2013-10 Issue:10 Volume:21 Page:1938-1949
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Sergijenko Ana,Langford-Smith Alexander,Liao Ai Y,Pickford Claire E,McDermott John,Nowinski Gabriel,Langford-Smith Kia J,Merry Catherine LR,Jones Simon A,Wraith J Edmond,Wynn Robert F,Wilkinson Fiona L,Bigger Brian W

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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3. Hematopoietic stem cell and gene therapy corrects primary neuropathology and behavior in mucopolysaccharidosis IIIA mice;Langford-Smith;Mol Ther,2012

4. Neuropathology in mouse models of mucopolysaccharidosis type I, IIIA and IIIB;Wilkinson;PLoS ONE,2012

5. Incidence and natural history of mucopolysaccharidosis type III in France and comparison with United Kingdom and Greece;Héron;Am J Med Genet A,2011

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