AAV-mediated photoreceptor transduction of the pig cone-enriched retina-Reference-Cited by-同舟云学术

AAV-mediated photoreceptor transduction of the pig cone-enriched retina

Published:2011-03-17 Issue:7 Volume:18 Page:637-645
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Mussolino C,della Corte M,Rossi S,Viola F,Di Vicino U,Marrocco E,Neglia S,Doria M,Testa F,Giovannoni R,Crasta M,Giunti M,Villani E,Lavitrano M,Bacci M L,Ratiglia R,Simonelli F,Auricchio A,Surace E M

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/gt20113.pdf

Reference42 articles.

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3. Cideciyan AV, Aleman TS, Boye SL, Schwartz SB, Kaushal S, Roman AJ et al. Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics. Proc Natl Acad Sci USA 2008; 105: 15112–15117.

4. Cideciyan AV, Hauswirth WW, Aleman TS, Kaushal S, Schwartz SB, Boye SL et al. Human RPE65 gene therapy for Leber congenital amaurosis: persistence of early visual improvements and safety at 1 year. Hum Gene Ther 2009; 20: 999–1004.

5. Cideciyan AV, Hauswirth WW, Aleman TS, Kaushal S, Schwartz SB, Boye SL et al. Vision 1 year after gene therapy for Leber's congenital amaurosis. N Engl J Med 2009; 361: 725–727.

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