Safety and Efficacy of Regional Intravenous (RI) Versus Intramuscular (IM) Delivery of rAAV1 and rAAV8 to Nonhuman Primate Skeletal Muscle-Reference-Cited by-同舟云学术

Safety and Efficacy of Regional Intravenous (RI) Versus Intramuscular (IM) Delivery of rAAV1 and rAAV8 to Nonhuman Primate Skeletal Muscle

Published:2008-07 Issue:7 Volume:16 Page:1291-1299
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Toromanoff Alice,Chérel Yan,Guilbaud Mickaël,Penaud-Budloo Magalie,Snyder Richard O,Haskins Mark E,Deschamps Jack-Yves,Guigand Lydie,Podevin Guillaume,Arruda Valder R,High Katherine A,Stedman Hansell H,Rolling Fabienne,Anegon Ignacio,Moullier Philippe,Le Guiner Caroline

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Muscle-directed gene transfer and transient immune suppression result in sustained partial correction of canine hemophilia B caused by a null mutation;Herzog;Mol Ther,2001

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