Design of Phosphorodiamidate Morpholino Oligomers (PMOs) for the Induction of Exon Skipping of the Human DMD Gene-Reference-Cited by-同舟云学术

Design of Phosphorodiamidate Morpholino Oligomers (PMOs) for the Induction of Exon Skipping of the Human DMD Gene

Published:2009-03 Issue:3 Volume:17 Page:554-561
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Popplewell Linda J,Trollet Capucine,Dickson George,Graham Ian R

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference36 articles.

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3. Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells;van Deutekom;Hum Mol Genet,2001

4. Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during pre-mRNA splicing in human muscle;Arechavala-Gomeza;Hum Gene Ther,2007

5. Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse;Mann;Proc Natl Acad Sci USA,2001

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