Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement-Reference-Cited by-同舟云学术

Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement

Published:2002-05 Issue:5 Volume:8 Page:423-425
ISSN:1078-8956
Container-title:Nature Medicine
language:en
Short-container-title:Nat Med

Author:

Aiuti Alessandro,Vai Sergio,Mortellaro Alessandra,Casorati Giulia,Ficara Francesca,Andolfi Grazia,Ferrari Giuliana,Tabucchi Antonella,Carlucci Filippo,Ochs Hans D.,Notarangelo Luigi D.,Roncarolo Maria Grazia,Bordignon Claudio

Publisher

Springer Science and Business Media LLC

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Link

http://www.nature.com/articles/nm0502-423.pdf

Reference11 articles.

1. Bordignon, C. et al. Gene therapy in peripheral blood lymphocytes and bone marrow for ADA- immunodeficient patients. Science 270, 470–475 (1995).

2. Blaese, R.M. et al. T lymphocyte–directed gene therapy for ADA-SCID: Initial trial results after 4 years. Science 270, 475–480 (1995).

3. Kohn, D.B. et al. Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency. Nature Med. 1, 1017–1023 (1995).

4. Hoogerbrugge, P.M. et al. Bone marrow gene transfer in three patients with adenosine deaminase deficiency. Gene Ther. 3, 179–183 (1996).

5. Onodera, M. et al. Successful peripheral T-lymphocyte-directed gene transfer for a patient with severe combined immune deficiency caused by adenosine deaminase deficiency. Blood 91, 30–36 (1998).

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