Beyond cystic fibrosis transmembrane conductance regulator therapy: a perspective on gene therapy and small molecule treatment for cystic fibrosis
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.nature.com/articles/s41434-019-0092-5.pdf
Reference84 articles.
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3. Sheppard DN, Welsh MJ. Structure and function of the CFTR chloride channel. Physiol Rev. 1999;79(1 Suppl):S23–45.
4. Schneider EK, Huang JX, Carbone V, Baker M, Azad MA, Cooper MA, et al. Drug-drug plasma protein binding interactions of ivacaftor. J Mol Recognit. 2015;28:339–48.
5. Tizzano EF, Buchwald M. CFTR expression and organ damage in cystic fibrosis. Ann Interna Med. 1995;123:305–8.
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