Gene therapy and gene correction: targets, progress, and challenges for treating human diseases
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
https://www.nature.com/articles/s41434-020-00197-8.pdf
Reference99 articles.
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4. Terheggen H. Unsuccessful trial of gene replacement in arginase deficiency. Z Kinderheilkd. 1975;119:1–3.
5. Blaese R, Culver K, Miller D, Carter C, Fleisher T, Clerici M. T lymphocyte-directed gene therapy for ADA-SCID: initial trial results after 4 years. Science. 1995;270:475.
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